Long-term use of lucerastat may protect kidneys in Fabry: Trial data
Long-term dosing with lucerastat, an experimental substrate reduction treatment from Idorsia, may slow the loss of kidney function in adults...
Fabry
Timing of Fabry enzyme replacement therapy tied to heart stability
Despite a delayed start until adulthood, enzyme replacement therapy (ERT) was associated with long-term cardiac stability in a man with...
I work hard to influence my health outcome with Fabry disease
For more than 20 years, I’ve had stage 3 chronic kidney disease. My Fabry disease also resulted in progressive heart...
ERT for Fabry disease can limit blood vessel damage in kidneys
Enzyme replacement therapy (ERT) may help limit damage to blood vessels in the kidneys of people with Fabry disease, a...
